Stargardt Disease Therapeutics Market - Global Industry Size, Share, Trends, Opportunity, and Forecast, 2020-2030F

Global Stargardt Disease Therapeutics Market was valued at USD 202.75 million in 2024 and is anticipated to project impressive growth in the forecast period with a CAGR of 7.50% through 2030. In Stargardt disease, an inherited eye condition, the macula, which plays a crucial role in clear central vision, is adversely affected. This condition typically manifests in childhood or adolescence and gradually leads to a decline in visual acuity.

While there are currently no approved treatments for Stargardt disease, significant progress has been made in the development of therapeutic approaches aimed at managing the condition and potentially arresting its progression. For instance, in 2023, WHO reported that over 2.2 billion people worldwide have vision impairment, with at least 1 billion cases preventable or unaddressed. The primary causes of blindness and vision loss globally are refractive errors and cataracts, highlighting the urgent need for improved eye care and preventive measures.

Key Market Drivers

Increased Prevalence and Awareness

The prevalence of Stargardt Disease has been on the rise, with an increasing number of individuals being diagnosed with this condition worldwide. While it remains a rare disease, the broader global population and improved diagnostic capabilities have led to more cases being identified. This heightened prevalence underscores the urgency of finding effective treatments and therapies for those affected. For instance, in 2025, Ascidian Therapeutics has received FDA authorization to begin a Phase 1/2 clinical trial for ACDN-01, its RNA editing therapy for Stargardt disease, a genetic eye disorder caused by ABCA4 mutations. Unlike traditional gene therapies, ACDN-01 rewrites RNA exons to restore healthy protein production, potentially benefiting many affected individuals.

Stargardt Disease primarily affects children and young adults, but the ageing population has also contributed to its increasing prevalence. As the global population continues to age, the demand for treatments for age-related eye conditions, including Stargardt Disease, is expected to grow significantly. This demographic shift amplifies the market potential for Stargardt Disease therapeutics.

Key Market Challenges

Limited Understanding of the Disease Mechanism

Despite significant progress, our understanding of the exact mechanisms underlying Stargardt Disease remains incomplete. This knowledge gap can impede the development of targeted therapies and necessitates ongoing research to uncover the complexities of the condition.

Key Market Trends

Gene Therapy Breakthroughs

Gene therapy is emerging as a promising avenue in the quest to treat Stargardt Disease. Researchers are conducting clinical trials to test the safety and efficacy of gene therapies that aim to replace or correct the faulty genes responsible for the condition. As trials progress, breakthroughs that bring gene therapy closer to becoming a viable treatment option are likely to come up.

Key Market Players

• Kubota Pharmaceutical Holdings Co Ltd
• IVERIC bio Inc
• Sanofi SA
• Alkeus Pharmaceuticals Inc
• Astellas Pharma Inc
• Cha Biotech Co Ltd/Old
• reVision Therapeutics, Inc.
• Biogen Inc
• F Hoffmann-La Roche AG
• Ocugen Inc

Report Scope:

In this report, the Global Stargardt Disease Therapeutics Market has been segmented into the following categories, in addition to the industry trends which have also been detailed below:

Stargardt Disease Therapeutics Market, By Drug Type:

• LBS-008
• Emixustat

Stargardt Disease Therapeutics Market, By Distribution Channel:

• Hospital Pharmacies
• Retail Pharmacies
• Online Pharmacies

Stargardt Disease Therapeutics Market, By Region:

• North America
• United States
• Canada
• Mexico
• Europe
• Germany
• United Kingdom
• France
• Italy
• Spain
• Asia-Pacific
• China
• Japan
• India
• Australia
• South Korea
• South America
• Brazil
• Argentina
• Colombia
• Middle East & Africa
• South Africa
• Saudi Arabia
• UAE
• Kuwait

Competitive Landscape

Company Profiles: Detailed analysis of the major companies present in the Global Stargardt Disease Therapeutics Market.

Available Customizations:

With the given market data, the publisher offers customizations according to a company's specific needs. The following customization options are available for the report.

Company Information

• Detailed analysis and profiling of additional market players (up to five).

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