+353-1-416-8900REST OF WORLD
+44-20-3973-8888REST OF WORLD
1-917-300-0470EAST COAST U.S
1-800-526-8630U.S. (TOLL FREE)
PTC Therapeutics - logo

PTC Therapeutics is a biopharmaceutical company that focuses on the development and commercialization of orally administered, small molecule drugs that target post-transcriptional control processes. The company's lead product candidate is Translarna (ataluren), which is for the treatment of of nonsense mutation Duchenne muscular dystrophy in ambulatory patients. It is currently in Phase III clinical trials to treat cystic fibrosis caused by nonsense mutations. The company was founded in 1998 and is headquartered in South Plainfield, New Jersey.

Duchenne Muscular Dystrophy Clinical Trial Analysis by Trial Phase, Trial Status, Trial Counts, End Points, Status, Sponsor Type and Top Countries, 2023 Update - Product Thumbnail Image

Duchenne Muscular Dystrophy Clinical Trial Analysis by Trial Phase, Trial Status, Trial Counts, End Points, Status, Sponsor Type and Top Countries, 2023 Update

  • Report
  • April 2023
  • 231 Pages
  • Global
From
Friedreich Ataxia Clinical Trial Analysis by Trial Phase, Trial Status, Trial Counts, End Points, Status, Sponsor Type and Top Countries, 2023 Update - Product Thumbnail Image

Friedreich Ataxia Clinical Trial Analysis by Trial Phase, Trial Status, Trial Counts, End Points, Status, Sponsor Type and Top Countries, 2023 Update

  • Report
  • January 2023
  • 92 Pages
  • Global
From
Novel Drug Reconstitution Systems Market by Type of Container, Fabrication Material, Physical State of Drug in Syringe and Cartridge, Physical State of Drug in Infusion Bag, Volume of Container, Key Geographical Regions: Industry Trends and Global Forecasts, 2021-2030 - Product Thumbnail Image

Novel Drug Reconstitution Systems Market by Type of Container, Fabrication Material, Physical State of Drug in Syringe and Cartridge, Physical State of Drug in Infusion Bag, Volume of Container, Key Geographical Regions: Industry Trends and Global Forecasts, 2021-2030

  • Report
  • September 2021
  • 325 Pages
  • Global
From
Huntington Disease Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Huntington Disease Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • November 2022
  • 299 Pages
  • Global
From
Duchenne Muscular Dystrophy - Market Insight, Epidemiology and Market Forecast -2030 - Product Thumbnail Image

Duchenne Muscular Dystrophy - Market Insight, Epidemiology and Market Forecast -2030

  • Report
  • October 2021
  • 250 Pages
  • Global
From
US Orphan Drugs Market, Drugs Sales, Price, Dosage & Clinical Trials Insight 2028 - Product Thumbnail Image

US Orphan Drugs Market, Drugs Sales, Price, Dosage & Clinical Trials Insight 2028

  • Report
  • July 2023
  • 3600 Pages
  • United States
From
Spinal Muscular Atrophy Treatment Market Size, Share & Trends Analysis Report By Type (Type1, Type 2), By Treatment (Gene Therapy, Drug), By Drug (Spinraza, Zolgensma), By Route Of Administration, By Region, And Segment Forecasts, 2022 - 2030 - Product Thumbnail Image

Spinal Muscular Atrophy Treatment Market Size, Share & Trends Analysis Report By Type (Type1, Type 2), By Treatment (Gene Therapy, Drug), By Drug (Spinraza, Zolgensma), By Route Of Administration, By Region, And Segment Forecasts, 2022 - 2030

  • Report
  • November 2022
  • 95 Pages
  • Global
From
Huntington`s Disease Therapeutics Market by Type, End-User - Global Forecast 2025-2030 - Product Thumbnail Image

Huntington`s Disease Therapeutics Market by Type, End-User - Global Forecast 2025-2030

  • Report
  • October 2024
  • 184 Pages
  • Global
From
Dravet Syndrome Treatment Market 2024-2028 - Product Thumbnail Image

Dravet Syndrome Treatment Market 2024-2028

  • Report
  • June 2024
  • 178 Pages
  • Global
From
Diabetic Gastroparesis Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Diabetic Gastroparesis Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • April 2022
  • 37 Pages
  • Global
From
Non-Alcoholic Steatohepatitis (NASH) (Gastrointestinal) - Drugs in Development, 2021 - Product Thumbnail Image

Non-Alcoholic Steatohepatitis (NASH) (Gastrointestinal) - Drugs in Development, 2021

  • Drug Pipelines
  • March 2021
  • Global
From
Amyotrophic Lateral Sclerosis Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Amyotrophic Lateral Sclerosis Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • September 2022
  • 672 Pages
  • Global
From
Parkinson's Disease Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Parkinson's Disease Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • September 2022
  • 1079 Pages
  • Global
From
Huntington's Disease Treatment Market Analysis & Forecast 2024-2034: Market By Drug; By Treatment; By End-user; and By Region - Product Thumbnail Image

Huntington's Disease Treatment Market Analysis & Forecast 2024-2034: Market By Drug; By Treatment; By End-user; and By Region

  • Report
  • October 2023
  • 145 Pages
  • Global
From
Peritoneal Cancer Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Peritoneal Cancer Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • June 2022
  • 925 Pages
  • Global
From
Friedreich Ataxia - Global Clinical Trials Review, 2024 - Product Thumbnail Image

Friedreich Ataxia - Global Clinical Trials Review, 2024

  • Report
  • October 2024
  • 101 Pages
  • Global
From
Leiomyosarcoma Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Leiomyosarcoma Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • April 2022
  • 152 Pages
  • Global
From
Huntington's Disease Treatment Market Forecasts from 2023 to 2028 - Product Thumbnail Image

Huntington's Disease Treatment Market Forecasts from 2023 to 2028

  • Report
  • November 2023
  • 145 Pages
  • Global
From
Drug-Resistant Epilepsy Market - Global Industry Size, Share, Trends Opportunity, and Forecast 2018-2028 - Product Thumbnail Image

Drug-Resistant Epilepsy Market - Global Industry Size, Share, Trends Opportunity, and Forecast 2018-2028

  • Report
  • October 2023
  • 178 Pages
  • Global
From
Glioblastoma Multiforme (GBM) Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Glioblastoma Multiforme (GBM) Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • December 2022
  • 1036 Pages
  • Global
From
Loading Indicator