Chapter 1. Methodology and Scope
1.1. Market Segmentation & Scope
1.2. Segment Definitions
1.2.1. Type
1.2.2. Diagnosis
1.2.3. Therapy
1.2.4. Estimates and forecasts timeline
1.3. Research Methodology
1.4. Information Procurement
1.4.1. Purchased database
1.4.2. GVR’s internal database
1.4.3. Secondary sources
1.4.4. Primary research
1.5. Information or Data Analysis
1.5.1. Data analysis models
1.6. Market Formulation & Validation
1.7. Model Details
1.7.1. Commodity flow analysis (Model 1)
1.7.2. Volume price analysis (Model 2)
1.8. List of Secondary Sources
1.9. List of Primary Sources
1.10. Objectives
Chapter 2. Executive Summary
2.1. Market Outlook
2.2. Segment Outlook
2.2.1. Type outlook
2.2.2. Diagnosis outlook
2.2.3. Therapy outlook
2.3. Competitive Insights
Chapter 3. U.S. Hemoglobinopathies Market Variables, Trends & Scope
3.1. Market Lineage Outlook
3.1.1. Parent market outlook
3.1.2. Related/ancillary market outlook
3.2. Market Dynamics
3.2.1. Market driver analysis
3.2.2. Market restraint analysis
3.3. U.S. Hemoglobinopathies Market Analysis Tools
3.3.1. Industry Analysis - Porter’s Five Forces
3.3.1.1. Supplier power
3.3.1.2. Buyer power
3.3.1.3. Substitution threat
3.3.1.4. Threat of new entrant
3.3.1.5. Competitive rivalry
3.3.2. PESTEL Analysis
3.3.2.1. Political landscape
3.3.2.2. Technological landscape
3.3.2.3. Economic landscape
Chapter 4. U.S. Hemoglobinopathies Market: Type Estimates & Trend Analysis
4.1. Type Market Share, 2023 & 2030
4.2. Segment Dashboard
4.3. U.S. Hemoglobinopathies Market by Type Outlook
4.4. Market Size & Forecasts and Trend Analyses, 2018 to 2030 for the Following
4.4.1. Thalassemia
4.4.1.1. Market estimates and forecasts 2018 to 2030 (USD Million)
4.4.2. Sickle cell disease
4.4.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
4.4.3. Other Hb variants
4.4.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
Chapter 5. U.S. Hemoglobinopathies Market: Diagnosis Estimates & Trend Analysis
5.1. Diagnosis Market Share, 2023 & 2030
5.2. Segment Dashboard
5.3. U.S. Hemoglobinopathies Market by Diagnosis Outlook
5.4. Market Size & Forecasts and Trend Analyses, 2018 to 2030 for the Following
5.4.1. Thalassemia
5.4.1.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.2. Alpha
5.4.1.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.2.2. Blood test
5.4.1.2.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.2.3. Genetic test
5.4.1.2.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.2.4. Prenatal genetic test
5.4.1.2.4.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.2.5. Pre-implantation genetic test
5.4.1.2.5.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.2.6. Electrophoresis
5.4.1.2.6.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.2.7. Others
5.4.1.2.7.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.3. Beta
5.4.1.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.3.2. Blood test
5.4.1.3.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.3.3. Genetic test
5.4.1.3.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.3.4. Prenatal genetic test
5.4.1.3.4.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.3.5. Pre-implantation genetic test
5.4.1.3.5.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.3.6. Electrophoresis
5.4.1.3.6.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.1.3.7. Others
5.4.1.3.7.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.2. Sickle cell disease
5.4.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.2.2. Blood test
5.4.2.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.2.3. Genetic test
5.4.2.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.2.4. Prenatal genetic test
5.4.2.4.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.2.5. Electrophoresis
5.4.2.5.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.2.6. Others
5.4.2.6.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.3. Hb variants
5.4.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.3.2. Blood test
5.4.3.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.3.3. Genetic test
5.4.3.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.3.4. Prenatal genetic test
5.4.3.4.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.3.5. Electrophoresis
5.4.3.5.1. Market estimates and forecasts 2018 to 2030 (USD Million)
5.4.3.6. Others
5.4.3.7. Market estimates and forecasts 2018 to 2030 (USD Million)
Chapter 6. U.S. Hemoglobinopathies Market: Therapy Estimates & Trend Analysis
6.1. Therapy Market Share, 2023 & 2030
6.2. Segment Dashboard
6.3. U.S. Hemoglobinopathies Market by Therapy Outlook
6.4. Market Size & Forecasts and Trend Analyses, 2018 to 2030 for the Following
6.4.1. Thalassemia
6.4.1.1. Market estimates and forecasts 2018 to 2030, (USD million)
6.4.1.2. Alpha
6.4.1.2.1. Market estimates and forecasts 2018 to 2030, (USD million)
6.4.1.2.2. Blood transfusion
6.4.1.2.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.1.2.2.2. Iron chelation therapy
6.4.1.2.2.3. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.1.2.3. Bone marrow transplant
6.4.1.2.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.1.2.4. Others
6.4.1.2.4.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.1.3. Beta
6.4.1.3.1. Market estimates and forecasts 2018 to 2030, (USD million)
6.4.1.3.2. Blood transfusion
6.4.1.3.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.1.3.2.2. Iron chelation therapy
6.4.1.3.2.3. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.1.3.3. Bone marrow transplant
6.4.1.3.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.1.3.4. Others
6.4.1.3.4.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.2. Sickle Cell Disease
6.4.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.2.2. Blood transfusion
6.4.2.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.2.3. Hydroxyurea
6.4.2.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.2.4. Bone marrow transplant
6.4.2.4.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.2.5. Others
6.4.2.5.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.3. (Hb) Variants
6.4.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.3.2. Blood transfusion
6.4.3.2.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.3.3. Hydroxyurea
6.4.3.3.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.3.4. Bone marrow transplant
6.4.3.4.1. Market estimates and forecasts 2018 to 2030 (USD Million)
6.4.3.5. Others
6.4.3.6. Market estimates and forecasts 2018 to 2030 (USD Million)
Chapter 7. Competitive Landscape
7.1. Recent Developments & Impact Analysis, By Key Market Participants
7.2. Company/Competition Categorization
7.3. Vendor Landscape
7.3.1. List of key distributors and channel partners
7.3.2. Key customers
7.3.3. Key company heat map analysis, 2023
7.4. Company Profiles
7.4.1. Sangamo Therapeutics, Inc.
7.4.1.1. Company overview
7.4.1.2. Financial performance
7.4.1.3. Product benchmarking
7.4.1.4. Strategic initiatives
7.4.2. Global Blood Therapeutics, Inc.
7.4.2.1. Company overview
7.4.2.2. Financial performance
7.4.2.3. Product benchmarking
7.4.2.4. Strategic initiatives
7.4.3. bluebird bio, Inc.
7.4.3.1. Company overview
7.4.3.2. Financial performance
7.4.3.3. Product benchmarking
7.4.3.4. Strategic initiatives
7.4.4. Emmaus Life Sciences Inc.
7.4.4.1. Company overview
7.4.4.2. Financial performance
7.4.4.3. Product benchmarking
7.4.4.4. Strategic initiatives
7.4.5. Pfizer, Inc.
7.4.5.1. Company overview
7.4.5.2. Financial performance
7.4.5.3. Product benchmarking
7.4.5.4. Strategic initiatives
7.4.6. Novartis AG
7.4.6.1. Company overview
7.4.6.2. Financial performance
7.4.6.3. Product benchmarking
7.4.6.4. Strategic initiatives
7.4.7. Prolong Pharmaceuticals, LLC
7.4.7.1. Company overview
7.4.7.2. Financial performance
7.4.7.3. Product benchmarking
7.4.7.4. Strategic initiatives
7.4.8. Bioverativ Inc.
7.4.8.1. Company overview
7.4.8.2. Financial performance
7.4.8.3. Product benchmarking
7.4.8.4. Strategic initiatives
7.4.9. Celgene Corp.
7.4.9.1. Company overview
7.4.9.2. Financial performance
7.4.9.3. Product benchmarking
7.4.9.4. Strategic initiatives
List of Tables
Table 1 List of abbreviations
Table 2 U.S. hemoglobinopathies market, by type, 2018-2030 (USD Million)
Table 3 U.S. hemoglobinopathies market, by diagnosis, 2018-2030 (USD Million)
Table 4 U.S. hemoglobinopathies market, by therapy, 2018-2030 (USD Million)
Table 5 U.S. thalassemia market, by diagnosis, 2018-2030 (USD Million)
Table 6 U.S. hemoglobinopathies market, by therapy, 2018-2030 (USD Million)
Table 7 U.S. alpha thalassemia market, by diagnosis, 2018-2030 (USD Million)
Table 8 U.S. beta thalassemia market, by diagnosis, 2018-2030 (USD Million)
Table 9 U.S. thalassemia market, by therapy, 2018-2030 (USD Million)
Table 10 U.S. alpha thalassemia market, by therapy, 2018-2030 (USD Million)
Table 11 U.S. beta thalassemia market, by therapy, 2018-2030 (USD Million)
Table 12 U.S. sickle cell disease market, by diagnosis, 2018-2030 (USD Million)
Table 13 U.S. sickle cell disease market, by therapy, 2018-2030 (USD Million)
Table 14 U.S. Hb Variants market, by diagnosis, 2018-2030 (USD Million)
Table 15 U.S. hemoglobinopathies market, by region, 2018-2030 (USD Million)
List of Figures
Figure 1 Market research process
Figure 2 Data triangulation techniques
Figure 3 Primary research pattern
Figure 4 Market research approaches
Figure 5 Value-chain-based sizing & forecasting
Figure 6 QFD modeling for market share assessment
Figure 7 Market formulation & validation
Figure 8 U.S. hemoglobinopathies market: market outlook
Figure 9 U.S. hemoglobinopathies competitive insights
Figure 10 Parent market outlook
Figure 11 Related/ancillary market outlook
Figure 12 Penetration and growth prospect mapping
Figure 13 Industry value chain analysis
Figure 14 U.S. hemoglobinopathies market driver impact
Figure 15 U.S. hemoglobinopathies market restraint impact
Figure 16 U.S. hemoglobinopathies market strategic initiatives analysis
Figure 17 U.S. hemoglobinopathies market: Type movement analysis
Figure 18 U.S. hemoglobinopathies market: Type outlook and key takeaways
Figure 19 Thalassemia market estimates and forecasts, 2018-2030 (USD Million)
Figure 20 Sickle cell diseases market estimates and forecasts, 2018-2030 (USD Million)
Figure 21 Other Hb variants estimates and forecasts, 2018-2030 (USD Million)
Figure 22 U.S. hemoglobinopathies Market: Diagnosis movement Analysis
Figure 23 U.S. hemoglobinopathies market: Diagnosis outlook and key takeaways
Figure 24 Thalassemia market estimates and forecasts, 2018-2030 (USD Million)
Figure 25 Alpha market estimates and forecasts, 2018-2030 (USD Million)
Figure 26 Blood test market estimates and forecasts, 2018-2030 (USD Million)
Figure 27 Genetic test market estimates and forecasts, 2018-2030 (USD Million)
Figure 28 Prenatal genetic test market estimates and forecasts, 2018-2030 (USD Million)
Figure 29 Pre-implantation genetic test market estimates and forecasts, 2018-2030 (USD Million)
Figure 30 Electrophoresis market estimates and forecasts, 2018-2030 (USD Million)
Figure 31 Other market estimates and forecasts, 2018-2030 (USD Million)
Figure 32 Beta market estimates and forecasts, 2018-2030 (USD Million)
Figure 33 Blood test market estimates and forecasts, 2018-2030 (USD Million)
Figure 34 Genetic test market estimates and forecasts, 2018-2030 (USD Million)
Figure 35 Prenatal genetic test market estimates and forecasts, 2018-2030 (USD Million)
Figure 36 Pre-implantation genetic test market estimates and forecasts, 2018-2030 (USD Million)
Figure 37 Electrophoresis market estimates and forecasts, 2018-2030 (USD Million)
Figure 38 Other market estimates and forecasts, 2018-2030 (USD Million)
Figure 39 Sickle cell disease market estimates and forecasts, 2018-2030 (USD Million)
Figure 40 Blood test market estimates and forecasts, 2018-2030 (USD Million)
Figure 41 Genetic test market estimates and forecasts, 2018-2030 (USD Million)
Figure 42 Prenatal genetic test market estimates and forecasts, 2018-2030 (USD Million)
Figure 43 Electrophoresis market estimates and forecasts, 2018-2030 (USD Million)
Figure 44 Others market estimates and forecasts, 2018-2030 (USD Million)
Figure 45 (Hb) variants market estimates and forecasts, 2018-2030 (USD Million)
Figure 46 Blood test market estimates and forecasts, 2018-2030 (USD Million)
Figure 47 Genetic test market estimates and forecasts, 2018-2030 (USD Million)
Figure 48 Prenatal genetic test market estimates and forecasts, 2018-2030 (USD Million)
Figure 49 Electrophoresis market estimates and forecasts, 2018-2030 (USD Million)
Figure 50 Others market estimates and forecasts, 2018-2030 (USD Million)
Figure 51 U.S. hemoglobinopathies Market: Therapy movement Analysis
Figure 52 U.S. hemoglobinopathies market: Therapy outlook and key takeaways
Figure 53 Thalassemia market estimates and forecasts, 2018-2030 (USD Million)
Figure 54 Alpha market estimates and forecasts, 2018-2030 (USD Million)
Figure 55 Blood transfusion market estimates and forecasts, 2018-2030 (USD Million)
Figure 56 Iron chelation therapy market estimates and forecasts, 2018-2030 (USD Million)
Figure 57 Bone marrow transplant test market estimates and forecasts, 2018-2030 (USD Million)
Figure 58 Others market estimates and forecasts, 2018-2030 (USD Million)
Figure 59 Beta market estimates and forecasts, 2018-2030 (USD Million)
Figure 60 Blood transfusion market estimates and forecasts, 2018-2030 (USD Million)
Figure 61 Iron chelation therapy market estimates and forecasts, 2018-2030 (USD Million)
Figure 62 Bone marrow transplant test market estimates and forecasts, 2018-2030 (USD Million)
Figure 63 Others market estimates and forecasts, 2018-2030 (USD Million)
Figure 64 Sickle cell disease market estimates and forecasts, 2018-2030 (USD Million)
Figure 65 Blood transfusion market estimates and forecasts, 2018-2030 (USD Million)
Figure 66 Hydroxyurea market estimates and forecasts, 2018-2030 (USD Million)
Figure 67 Bone marrow transplant test market estimates and forecasts, 2018-2030 (USD Million)
Figure 68 Others market estimates and forecasts, 2018-2030 (USD Million)
Figure 69 (Hb) variants market estimates and forecasts, 2018-2030 (USD Million)
Figure 70 Blood transfusion market estimates and forecasts, 2018-2030 (USD Million)
Figure 71 Hydroxyurea market estimates and forecasts, 2018-2030 (USD Million)
Figure 72 Bone marrow transplant test market estimates and forecasts, 2018-2030 (USD Million)
Figure 73 Others market estimates and forecasts, 2018-2030 (USD Million)
Figure 74 U.S. hemoglobinopathies market: regional movement analysis
Figure 75 U.S. hemoglobinopathies market: regional outlook and key takeaways
Figure 76 West market estimates and forecasts, 2018-2030 (USD Million)
Figure 77 Midwest market estimates and forecasts, 2018-2030 (USD Million)
Figure 78 Northeast market estimates and forecasts, 2018-2030 (USD Million)
Figure 79 Southwest market estimates and forecasts, 2018-2030 (USD Million)
Figure 80 Southeast market estimates and forecasts, 2018-2030 (USD Million)